♜ : lead (or co-lead) author is a student-advisee of Marco Carone (or was when work was initiated)
♝ : authors listed alphabetically to reflect equal contributions
♞ : first two authors made an equal contribution


  1. Follmann, D., Fintzi, J., Fay, M.P., Janes, H.E., Baden, L., El Sahly, H., Fleming, T.R., Mehrotra, D.V., Carpp, L.N., Juraska, M., Benkeser, D., Donnell, D., Fong, Y., Han, S., Hirsch, I., Huang, Y., Huang, Y., Hyrien, O., Luedtke, A., Carone, M., Nason, M., Vandebosch, A., Zhou, H., Cho, I., Gabriel, E., Kublin, J., Cohen, M.S., Corey, L., Gilbert, P.B., Neuzil, K.M., 2021+. A deferred-vaccination design to assess durability of COVID-19 vaccine effect after the placebo group is vaccinated. Annals of Internal Medicine, in press.
  2. Lind, M., Mooney, S.J., Carone, M., Althouse, B.M., Liu, C., Evans, L.E., Patel, K., Vo., P., Pergam, S.A., Phipps, A.I., 2021+. Development and validation of a machine learning model to predict bacterial sepsis decision among immunocompromised stem cell transplant recipients. JAMA Network Open, in press.
  3. Meisner, A., Carone, M., Pepe, M.S., Kerr, K.F., 2021+. Combining biomarkers by maximizing the true positive rate for a fixed false positive rate. Biometrical Journal, accepted.
  4. Hwang, P.H., Longstreth, W.T., Thielke, S.M., Francis, C.E., Carone, M., Kuller, L.H., Fitzpatrick, A.L., 2021+. Ophtalmic conditions associated with dementia risk: the Cardiovascular Health Study. Alzheimer’s & Dementia, in press.
  5. ♜ Qiu, H., Luedtke, A.R., Carone, M., 2020+. Universal sieve-based strategies for efficient estimation using machine learning tools. Bernoulli, accepted.
  6. Shaffer, R.M., Li, G., Adar, S.D., Keened, C.D., Latimer, C., Crane, P.K., Larson, E.B., Carone, M., Sheppard, L., 2020+. Fine particulate matter and markers of Alzheimer’s Disease neuropathology at autopsy in a Puget Sound cohort. The Journal of Alzheimer’s Disease, accepted.
  7. Lyons, V.H., Floyd, A.S., Griffin, E., Wang, J., Hajat, A., Carone, M., Benkeser, D., Whiteside, L, Haggerty, K.P., Rivara, F.P., Rowhani-Rahbar, A., 2020+. Helping individuals with firearm injuries: a cluster randomized trial. The Journal of Trauma, accepted.
  8. Mehrotra, D.V., Janes, H.E., Fleming, T.R., Annunziato, P.W., Neuzil, K.M., Carpp, L.N., Benkeser, D., Brown, E.R., Carone, M., Cho, I., Donnell, D., Fay, M.P., Fong, Y., Han, S., Hirsch, I., Huang, Y., Hyrien, O., Juraska, M., Luedtke, A., Nason, M., Vandebosch, A., Zhou, H., Cohen, M.S., Corey, L., Hartzel, J., Follmann, D. Gilbert, P.B, 2020+. Clinical endpoints for evaluating efficacy in COVID-19 vaccine trials. Annals of Internal Medicine, accepted.
  9. ♜ Westling, T., Gilbert, P.B., Carone, M., 2020+. Causal isotonic regression. Journal of the Royal Statistical Society: Series B, accepted.
  10. ♜ Williamson, B., Gilbert, P.B., Carone, M., Simon, N., 2020+. Rejoinder to "Nonparametric variable importance assessment using machine learning techniques". Biometrics, accepted.
  11. ♜ Williamson, B., Gilbert, P.B., Carone, M., Simon, N., 2020+. Nonparametric variable importance assessment using machine learning techniques. Biometrics, accepted with discussion.
  12. ♜ Qiu, H., Carone, M., Sadikova, E., Petukhova, M., Kessler, R., Luedtke, A.R., 2020+. Rejoinder to ''Optimal individualized decision rules using instrumental variable methods''. Journal of the American Statistical Association, accepted.
  13. ♜ Qiu, H., Carone, M., Sadikova, E., Petukhova, M., Kessler, R., Luedtke, A.R., 2020+. Optimal individualized decision rules using instrumental variable methods. Journal of the American Statistical Association, accepted with discussion.
  14. ♜ Westling, T., van der Laan, M.J., Carone, M., 2020. Correcting an estimator of a multivariate monotone function using isotonic regression. Electronic Journal of Statistics, 14(2):3032-3069.
  15. ♜ Westling, T., Carone, M., 2020. A unified study of nonparametric inference for monotone functions. Annals of Statistics, 48(2):1001-1024.
  16. Luedtke, A.R., Carone, M., Simon, N., Sofrygin, O., 2020. Learning to learn from data: using deep adversarial learning to construct optimal statistical procedures. Science Advances, 6(9).
  17. ♜ Whitney, D., Shojaie, A., Carone, M., 2019. Models as (deliberate) approximations. Statistical Science, 34(4):591-598.
  18. Harbison, R., Gray, A., Westling, T., Carone, M., Rodriguez, C., Futran, N., Cannon, R., Houlton, J., 2019. The role of elective neck dissection in high-grade parotid malignancy: a hospital-based cohort study. The Laryngoscope, in press (available online).
  19. ♜ Lyons, V., Kernic, M., Rowhani-Rahbar, A., Holt, V., Carone, M., 2019. Use of multiple failure models in injury epidemiology: a case study of arrest and intimate partner violence recidivism in Seattle, WA. Injury Epidemiology, 6:36.
  20. Shinohara, R.T., Shou, H., Carone, M., Schultz, R., Parker, D., Verma, R., 2019. Distance-based analysis of variance for brain connectomics. Biometrics, in press (available online).
  21. Carone, M., Dominici, F., Sheppard, L., 2019. In pursuit of evidence in air pollution epidemiology: the role of causally-driven data science. Epidemiology, 31(1):1-6.
  22. Magaret, C.A., Benkeser, D.C., Williamson, B.D., Borate, B.R., Carpp, L.N., Georgiev, I.S., Setliff, I., Dingens, A.S., Simon, N., Carone, M., Simpkins, C., Montefiori, D., Alter, G., Yu, W.H., Juraska, M., Edlefsen, P.T., Karuna, S., Mgodi, N.M., Edugupanti, S., Gilbert, P.B., 2019. Prediction of VRC01 neutralization sensitivity by HIV-1 gp160 sequence features. PLoS Computational Biology, in press (available online).
  23. Camargo, A., Youssem, K., Westling, T., Carone, M., Youssem, D.M., 2019. Ethical dilemmas in radiology: survey of opinions and experiences. American Journal of Roentgenology, 213(6):1274-1283.
  24. ♜ Benkeser, D.C., Gilbert, P.B., Carone, M., 2019. Estimating and testing vaccine sieve effects using machine learning. Journal of the American Statistical Association, 114(527):1038-1049.
  25. Carone, M., Luedtke, A.R., van der Laan, M.J., 2019. Toward computerized efficient estimation in infinite-dimensional models. Journal of the American Statistical Association, 114(527):1174-1190.
  26. Luedtke, A.R., Carone, M., van der Laan, M.J., 2019. An omnibus nonparametric test of equality in distribution for unknown functions. Journal of the Royal Statistical Society: Series B, 81(1):75-99.
  27. Jang M., Sakadi F., Tassiou N.R., Abass C.F., Grundy S.J., Woga A., Kenda B.A., Lamine C.M., Talibé B.A., Qiu H., Cohen J.M., Carone M., Mateen F.J., 2018. Impact of Poorly Controlled Epilepsy in the Republic of Guinea. Seizure: European Journal of Epilepsy, 61:71-77.
  28. ♜ Feng, J., Williamson, B., Carone, M., Simon, N., 2018. Nonparametric variable importance using an augmented neural network with multi-task learning. Proceedings of the 35th International Conference on Machine Learning, 80:1496-1505.
  29. Carone, M., Diaz, I.M., van der Laan, M.J., 2018. Higher-order targeted loss-based learning. Chapter 26 of Targeted Learning in Data Science: Causal Inference for Complex Longitudinal Studies. Springer.
  30. ♜ Benkeser, D.C., Carone, M., Gilbert, P.B., 2018. Targeted estimation of cumulative incidence in settings with competing risks. Chapter 11 of Targeted Learning in Data Science: Causal Inference for Complex Longitudinal Studies. Springer.
  31. ♜ Benkeser, D.C., Carone, M., van der Laan, M.J., Gilbert, P.B., 2017. Nonparametric doubly-robust inference on the average treatment effect. Biometrika, 104(4):863-880.
  32. Mateen, F.J., Carone, M., Tshering, L., Dorji, C., Dema, U., Grundy, S.J., Ram, D., Nirola, D.K., 2017. Area catechu and seizures among people with epilepsy in Bhutan: an observational study. Epilepsy & Behavior, 74(Sep 2017):76-80.
  33. Scharfstein, D.O., McDermott, A., Diaz, I.M., Carone, M., Lunardon, N., Turkoz, I., 2017. Global sensitivity analysis for repeated measures studies with informative drop-out: a semiparametric approach. Biometrics, 74(1):207-219.
  34. Pirracchio, R., Carone, M., 2017. The Balance Super Learner: a robust adaptation of the Super Learner to improve average treatment effect estimation based on propensity score matching. Statistical Methods in Medical Research, 27(8):2504-2518.
  35. ♜ Benkeser, D.C., Carone, M., Gilbert, P.B., 2017. Improved estimation of cumulative incidence of rare outcomes. Statistics in Medicine, 37(2):280-293.
  36. Koelman, D.L.H., Benkeser, D.C., Xu, Y., Neo, X., Tan, K., Katsuno, M., Sobue, G., Natsume, J., Chahin, S., Mar, S.S., Venkatesan, W., Chitnis, T., Hoganson, G.M., Yeshokumar, A.K., Barreras, P., Majmudar, B., Carone, M., Mateen, F.J., 2016. Acute disseminated encephalomyelitis in China, Singapore and Japan: comparison with the USA. European Journal of Neurology, 24(2):391-396.
  37. Stankiewicz, K., Cohen, M., Carone, M., Sevinc, G., Nagy, P.G., Lewin, J.S., Yousem, D.Y., Babiarz, L.S., 2016. Comparing preliminary and final neuroradiology reports: what are the factors that determine the differences? American Journal of Neuroradiology, 37(11)1977-1982.
  38. Koelman, D.L.H., Chahin, S., Mar, S.S., Venkatesan, A., Hoganson, G.M., Yeshokumar, A.K., Barreras, P., Majmudar, B., Klein, J.P., Chitnis, T., Benkeser, D.C., Carone, M., Mateen, F.J., 2016. Acute disseminated encephalomyelitis in 228 patients: a retrospective, multicenter U.S. study. Neurology, 86(22):2085-2093.
  39. Diaz, I.M., Carone, M., van der Laan, M.J., 2016. Second-order inference for the mean of a variable missing at random. The International Journal of Biostatistics, 12(1):333-349.
  40. ♞ Luedtke, A.R., Carone, M., van der Laan, M.J., 2015. Discussion of “Deductive derivation and Turing-computerization of semi parametric efficient estimation” by Frangakis et al. Biometrics, 71(4):875-879.
  41. Huntley, J.M., Carone, M., Yousem, D.M., Babiarz, L.S., 2015. Opportunities for targeted education: critical neuroradiological findings missed or misinterpreted by residents and fellows. American Journal of Roentgenology, 205(6):1155-1159.
  42. Azab, M., Carone, M., Ying, S.H., Yousem, D.M., 2015. Mesial temporal sclerosis: accuracy of NeuroQuant versus neuroradiologist? American Journal of Neuradiology, 36(8):1400-1406.
  43. Wahlster, S., Wijdicks, E.F.M., Patel, P.V., Greer, D.M., Hemphill, J.C., Carone, M., Mateen, F.J., 2015. Brain death declaration practices and perceptions worldwide. Neurology, 85(18):1870-1879.
  44. Pirracchio, R., Petersen, M.L., Carone, M., Resche Rigon, M., Chevret, S., van der Laan, M.J., 2015. Mortality prediction in the ICU: can we do better? Results from the Super ICU Learner Algorithm (SICULA) project, a population-based study. The Lancet Respiratory Medicine, 4,(2):136-145.
  45. Mateen, F.J., Geer, J.P., Frick, K., Carone, M., 2014. Neurological disorders in Medicaid- versus privately-insured children and working age adults. Neurology: Clinical Practice, 4(2):136-145.
  46. Carone, M., Asgharian, M., Jewell, N.P., 2014. Estimating the lifetime risk of dementia in the Canadian population using cross-sectional survival data. Journal of the American Statistical Association, 109:(505):24-35.
  47. Pirracchio, R., Carone, M., Resche Rigon, M., Caruana, E., Mebazaa, A., Chevret, S., 2013. Propensity score estimators for the average treatment effect and the average treatment effect on the treated may yield very different estimates. Statistical Methods in Medical Research, 25(5):1938-1954.
  48. Carone, M., Asgharian, M., Wang, M.C., 2012. Nonparametric incidence estimation from prevalent cohort survival data. Biometrika, 99(3):599-613. [supplementary material]
  49. ♝ Asgharian, M., Carone, M., Fakoor, V., 2012. Large-sample study of the kernel density estimators under multiplicative censoring. Annals of Statistics, 40(1):159-187. [supplementary material]
  50. Carone, M., Petersen, M., van der Laan, M.J., 2012. Targeted minimum loss-based estimation of a causal effect using interval-censored time-to-event data. Chapter 8 of Interval-censored time-to-event data: methods and applications. Chapman & Hall/CRC.
  51. Mateen, F.J., Niu, J.W., Gao, S., Li, S.W., Carone, M., Wijdicks, E.F.M., Xu, W.H., 2012. Causes and outcomes of persistent vegetative state in a Chinese versus American referral hospital. Electronic publication ahead of print, Neurocritical Care.
  52. Intrapiromkul, J., Aygun, N., Tunkel, D.E., Carone, M., Yousem, D.M. Inner ear anomalies seen on CT images in patients with Down syndrome. Electronic publication ahead of print, Pediatric Radiology.
  53. Mateen, F.J., Shinohara, R., Carone, M., Jacobson, L., Sacktor, N., 2012. Neurological disorders incidence in HIV+ and HIV- men: Multicenter AIDS Cohort Study, 1996-2011. Neurology, 79(18):1873-1880.
  54. Mateen, F.J., Carone, M., Haskew, C., Spiegel, P., 2012. Reportable neurological diseases in refugee camps in 19 countries. Neurology, 79(9):937-940.
  55. Mateen, F.J., Carone, M., Al-Saedy, H., Nyce, S., Mutuerandu, T., Ghosn, J., Jatoi, A., 2012. Cancer diagnoses in Iraqi refugees. Acta Oncologica, 51(7):950-951.
  56. Mateen, F.J., Carone, M., Al-Saedy, H., Nyce, S., Ghosn, J., Mutuerandu, T., Black, R.E., 2012. Medical conditions among Iraqi refugees in Jordan: data from the United Nations Refugee Assistance Information System. Bulletin of the World Health Organization, 90(6):444-451.
  57. Mateen, F.J., Carone, M., Alam, N., Streatfield, P.K., Black, R., 2012. A population-based case-control study of 1250 stroke deaths in rural Bangladesh. European Journal of Neurology, 19(7):999-1006.
  58. Viertel, V.G., Babiarz, L.S., Carone, M., Lewin, J.S., Yousem, D.M., 2012. Quality control in neuroradiology: impact of trainees on discrepancy rates. American Journal of Neuroradiology, 33(6):1032-1036.
  59. Khalid, L., Carone, M., Dumrongpisutikul, N., Intrapiromkul, J., Yousem, D.M., 2012. Imaging characteristics of oligodendrogliomas that predict grade. American Journal of Neuroradiology, 33(5):852-857.
  60. Passerini, L.D., Casey, G.J., Tran Cong, D., Luong Ba, P., Tran Quang, P., Carone, M., Biggs, B.A., Montresor, A., 2012. Increased birth weight associated with regular pre-pregnancy deworming and weekly iron-folic acid supplementation for Vietnamese women. PLoS Neglected Tropical Diseases, 6(4):e1608.
  61. Mateen, F.J., Carone, M., Nyce, S., Ghosn, J., Mutureandu, T., Al-Saedy, H., Lowenstein, D.S., Burnham, G., 2012. Neurological disorders in Iraqi refugees in Jordan: data from the United Nations Refugee Assistance Information System. Journal of Neurology, 259(4):694-701.
  62. Anwar, Z., Zan, E., Carone, M., Ozturk, A., Sozio, S., Yousem, D.M., 2011. Superficial temporal artery calcification in patients with end-stage renal disease: association with vascular risk factors and ischemic cerebrovascular disease. Indian Journal of Radiology and Imaging, 21(3):215-220.
  63. Wyse, J.M., Carone, M., Usatii, M., Paquin, S.C., Sahai, A., 2011. A randomized, double-blind, controlled trial of prophylactic endoscopic ultrasound-guided celiac plexus neurolysis (EUS-CPN) to prevent pain progression in patients with newly diagnosed, inoperable pancreatic cancer. Journal of Clinical Oncology, 29(26):3541-3546.
  64. Mateen, F.J., Muralidharan, R., Carone, M., van de Beek, D., Harrison, D., Clifford, D., Aksamit, A.J., Nath, A., 2011. Progressive multifocal leukoencephalopathy in transplant recipients. Annals of Neurology, 70(2): 305-322.
  65. Mateen F.J., Josephs, K.A., Trenerry, M.R., Devine, M.D.F., Weaver, A., Carone, M., White, R.D., 2011. Long-term cognitive outcomes following out-of-hospital cardiac arrest: a population-based study. Neurology, 77(15):1438-1445.
  66. Lo, S.S., Atceken, Z., Carone, M., Yousem, D.M., 2011. Vacuum phenomenon in sacroiliac joints – underreported finding. Clinical Imaging, 35(6):465-469.
  67. Mateen, F.J., Carone, M., Sorenson, M., 2010. Patients who survive five years or more with ALS in Olmsted County, 1925-2004. Journal of Neurology, Neurosurgery and Psychiatry, 81:1144-1146.
  68. Leibler, J.H., Carone, M., Silbergeld, E.K., 2010. Contribution of company affiliation and social contacts to risk estimates of between-farm transmission of avian influenza. PLoS ONE, 5(3):e9888.
  69. Zan, E., Yousem, D.M., Carone, M., Lewin, J.S., 2010. Second opinion consultations in neuroradiology: assessment of value. Radiology, 255(1):135-141.
  70. Mohajer, A., Trémier, A., Barrington, S., Martinez, J., Teglia, C., Carone, M., 2009. Microbial oxygen uptake in sludge as influenced by compost physical parameters. Waste Management, 29(8):2257-2264.


  1. ♜ Westling, T., Luedtke, A.R., Gilbert, P.B., Carone, M. Inference for treatment-specific survival curves using machine learning.
  2. Hudson, A., Carone, M., Shojaie, A. Inference on function-valued parameters using a restricted score test.
  3. ♜ Williamson, B., Gilbert, P.B., Simon, N., Carone, M. A unified approach for inference on algorithm-agnostic variable importance.
  4. Luedtke, A.R., Sofrygin, O., van der Laan, M.J., Carone, M. Sequential double robustness in longitudinal censoring models.